Areas of Focus · Peripheral neuropathies (including Charcot-Marie-Tooth disease) · Lysosomal storage disorders (including Sanfilippo syndrome and other ...

Gene therapy involves the introduction of new genes into cells, to restore or add gene expression, for the purpose of treating disease.

Designing the Next Generation of Gene Therapy Treatments · Development of gene therapy treatments to prevent vascular dysfunction in diabetic retinopathy.

Animal Models of Human Disease · Bioinformatics & Statistics · Cancer Genetics and Genomics · Cardiovascular Genetics · Clinical and Therapeutics · Development.

Gene Therapy of Muscular, Liver, Skin and Bone Disorders, and Familial Diabetes. Included in this section are Center Members and Associate Members, many of whom ...

Gene Therapy · Critical Care Research · Diabetes Mellitus · Extracellular Vesicles · Gene Therapy · Immunology · Musculoskeletal Disease · Osteoarthritis · Stem Cell ...

The emerging field of cell and gene therapies (CGT's) offers an unprecedented opportunity to treat diseases for which existing interventions are inadequate ...

Investigating the potential of gene therapy in treating autoimmune diseases. Developing biotechnological methods for producing environmentally friendly dyes.

The approach is broad, with potential treatment of diseases caused by recessive gene disorders (cystic fibrosis, hemophilia, muscular dystrophy, and sickle cell ...

FOCUSED RESEARCH TOPICS · 1. Behavioural genetics: Twin and family studies · 2. Cytogenetics: Karyotyping · 3. Epigenetics: Molecular basis · 4. Molecular genetics:.