20 окт. 2020 г. · This review discusses therapeutic strategies for the treatment of metachromatic leukodystrophy, as well as diagnostic methods and modeling of this pathology in ...

20 окт. 2020 г. · This review discusses therapeutic strategies for the treatment of metachromatic leukodystrophy, as well as diagnostic methods and modeling of this pathology in ...

20 окт. 2020 г. · This review discusses therapeutic strategies for the treatment of metachromatic leukodystrophy, as well as diagnostic methods and modeling of ...

The significant advance in technology has allowed timely diagnosis in patients suffering from LDM; however, they still do not have an effective treatment. Key ...

23 мая 2024 г. · Several treatment approaches are promising and include bone marrow or blood transplantation, gene therapy, enzyme replacement therapy, and cell therapy.

This document summarizes current guidance on the presymptomatic monitoring of children affected by MLD as well as the clinical management of symptomatic ...

Currently, there is no treatment available that reverses the development of characteristic neurological and systemic symptoms. Objective. Carry out an updated ...

6 мар. 2020 г. · Current treatment is aimed at preventing nerve damage, slowing progression of the disorder, preventing complications and providing supportive care. Не найдено: modeling | Нужно включить: modeling

Bone marrow stem cell-based gene transfer in a mouse model for metachromatic leukodystrophy: effects on visceral and nervous system disease manifestations.

This review discusses diagnostic process and efficacy of current and possible future therapies such as hematopoietic stem cell transplantation, enzyme ...